Overview
Chemotherapeutic agents for rare diseases are drugs used to treat conditions that affect fewer than 200,000 people in the United States. These drugs target the underlying genetic cause of the disease and are designed to inhibit or delay the progression of the condition. Examples include treatments for Huntington's disease, cystic fibrosis, and rare cancers. Chemotherapeutic agents are the primary form of treatment for these diseases and can improve quality of life and help extend life expectancy. They can also be used in combination with other treatments, such as surgery or radiation therapy, to provide a more effective approach.
Research published in this journal
No peer-reviewed research on this exact topic has been published in International Journal of Chemotherapy Research and Practice yet. Browse the journal →